Pharmacoeconomics

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Session · 31 of 35

Pharmacoeconomics

Pharmacoeconomic analysis informs reimbursement decisions with growing US uptake post-IRA. The session covers ICER value frameworks and controversies, EU EUnetHTA JCA implementation, NICE methods and evidence requirements, pharmacoeconomic modelling (Markov, partitioned survival, MAIC), HTA bodies globally (NICE, CADTH, IQWiG, HAS), and IRA Medicare negotiation impact on prices. Discussion addresses outcomes research methodologies, cost-effectiveness vs cost-utility analysis, patient-reported outcomes in value assessment, equity in pharmacoeconomic frameworks, and value-based contracting for gene therapies.

Topics covered in this session
  • ICER value frameworks
  • EU JCA implementation
  • NICE methods
  • Markov pharmacoeconomic modelling
  • HTA bodies globally
  • IRA price impact
  • Patient-reported outcomes value
  • Value-based gene therapy contracts